Homology Medicines, Inc., a genetic medicines company, focuses on transforming the lives of patients suffering from rare genetic diseases. Its proprietary platform is designed to utilize its human hematopoietic stem cell derived adeno-associated virus vectors (AAVHSCs) to deliver genetic medicines in vivo either through a gene therapy or nuclease-free gene editing for various genetic disorders. The company's various set of AAVHSCs allows company to target, through a single injection, a range of disease-relevant tissues, including the liver, central nervous system, peripheral nervous system, bone marrow, cardiac and skeletal muscle, and eye. Its lead product candidate is HMI-102, which is in Phase 2 pheNIX clinical trial, a gene therapy for the treatment of phenylketonuria (PKU) in adults. The company also develops HMI-103 for the treatment of PKU in pediatric patients; HMI-202 to treat metachromatic leukodystrophy; and HMI-203 for the treatment of mucopolysaccharidosis type II, as well as HMI-104 for the treatment of patients with paroxysmal nocturnal hemoglobinuria. Homology Medicines, Inc. was incorporated in 2015 and is headquartered in Bedford, Massachusetts.

Ms. Jodie Pope Morrison

Chief Executive Officer & Director

Dr. Shelia M. Violette Ph.D.

Co-founder, Chief Scientific Officer & President of Research

Ms. Maria  Marzilli M.P.H.

Executive Vice President of Corporate Strategy & Program Operations

Ms. Kathryn E. Golden M.B.A.

Head of Chemistry, Manufacturing & Controls

Dr. Jason A. Campagna M.D., Ph.D.

Chief Medical Officer

Mr. David  Appugliese J.D.

Senior Vice President & Head of People

Dr. Saul  Fink Ph.D.

Chief Technology Officer

Mr. Lee H. Kalowski M.B.A.

Chief Financial Officer, President & Treasurer

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Homology Medicines, Inc.

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